muscular dystrophy

  • child runs toward ball on beach
    medications

    Drug is first gene therapy for Duchenne muscular dystrophy

    A new drug is the first gene therapy approved to treat debilitating and fatal Duchenne muscular dystrophy in four- and five-year-old boys.
  • A young boy in a wheelchair looks into the background while outside.
    children's health

    Daily steroids are safe for kids with Duchenne muscular dystrophy

    Daily steroids are not only safe for children with Duchenne muscular dystrophy, they also slow the disease's progression, a new study shows.
  • Cells glowing in different colors on a black background
    muscular dystrophy

    Discovery could lead to Duchenne muscular dystrophy therapies

    Research into how chronic inflammation promotes muscle fibrosis could lead to new therapies for people with Duchenne muscular dystrophy, a fatal disease.
  • A little white mouse grabs the bars of its cage and pokes its head out the open door.
    muscles

    New approach prevents muscular dystrophy damage in mice

    Giving a boost to molecules involved in muscle repair could help stave off damage due to Duchenne muscular dystrophy, researchers report.
  • A crossstich of a broken heart mended with black thread
    heart disease

    Protein tweak may prevent DMD-related heart disease

    Altering 1 protein in the heart may prevent heart disease related to Duchenne muscular dystrophy, research in mice shows.
  • A lab mouse sits on a metal table with a researcher in gloves and a lab coat visible in the background
    genetic engineering

    CRISPR fix in mice may lead to muscular dystrophy therapy

    Using CRISPR to correct mutated muscle stem cells in mice may pave the way for lifelong treatments for people with Duchenne muscular dystrophy.
  • string of flags
    genes

    Can more ‘flags’ help CRISPR treat Duchenne muscular dystrophy?

    A new discovery may bring scientists a step closer to using the gene editing technique CRISPR to treat long-term chronic conditions like DMD.
  • Mobile Maestro app on phone - muscular dystrophy
    muscular dystrophy

    Exoskeleton app makes life with muscular dystrophy easier

    Controlling an exoskeleton with an app on his phone makes reading, shaving, and other tasks far less cumbersome for Zach Smith, who has Duchenne muscular dystrophy.
  • teen boy flexes arm
    steroids

    Taking steroids less often could ‘fix’ muscles

    Daily doses of steroids can cause muscle wasting. A study with mice shows weekly doses can actually do the opposite—repair them. Could it work for people?